Colección: TEMAS

Temas Cantidad
Acute infantile Gaucher disease; Motor regression; Hypotonia1
Fabry disease; Childhood; Enzyme replacement therapy1
Gastrointestinal Tract; Symptoms; Diagnosis; Child1
Heart; Lysomoal disease; Treatment1
Intractable Epilepsy; Antiepileptic drugs; Zonisamide1
Lysosomal Storage Diseases, Rheumatology, Bone pain; Arthropathy1
Lysosomal disorders; Diagnosis; Approach1
Lysosomal myopathy; Myopathy; Pompe; Acid maltase deficiency, Danon1
Mucopolysaccharidosis 1; Child; Diagnosis; Therapy1
No aplica10